Transcriptional profiling of iPSC-derived motor neurons from patients with the C9orf72 hexanucleotide repeat expansion and correction using antisense oligonucleotides as a potential therapeutic strategy for Amyotrophic Lateral Sclerosis
Transcriptional profiling of iPSC-derived motor neurons from patients with the C9orf72 hexanucleotide repeat expansion and correction using antisense oligonucleotides as a potential therapeutic strategy for Amyotrophic Lateral Sclerosis